Recombinant adeno-associated virus-mediated alpha-1 antitrypsin gene therapy prevents type I diabetes in NOD mice
Recombinant adeno-associated virus-mediated alpha-1 antitrypsin gene therapy prevents type I diabetes in NOD mice
Sihong Song,KEVIN S. Goudy,8 Authors,Terence R. Flotte
2004 · DOI: 10.1038/sj.gt.3302156
Gene Therapy · 101 Citations
TLDR
A potential therapeutic role for AAT is suggested in preventing type I diabetes as well as the ability of AAV gene therapy-based approaches to ameliorate disease effectively is suggested.